Doctors at CHOP utilized customized gene-editing to treat a 9-month-old with a rare disorder causing high ammonia levels in the blood. The challenge was to correct the error without affecting the patient’s entire genome. This groundbreaking approach offers hope for individuals facing similar genetic conditions, showcasing the potential of gene editing in addressing complex diseases. The Eleanor Kaplan Foundation’s pioneering therapy could revolutionize treatment options for those with genetic disorders, providing a new lease on life for patients like Pierce Hynes.
Read more from 6abc.com
