Category: Lipid Nanoparticles for Gene Therapy

First Customized CRISPR Treatment for Baby

In a groundbreaking development, a baby received the first customized CRISPR treatment after a collaboration involving academic and company scientists, including Aldevron, Integrated DNA Technologies, Acuitas Therapeutics, and Danaher Corporation. The therapy, produced by Aldevron, targeted a rare genetic mutation threatening infants like KJ, with guidance from IDT’s RNA genetic sequence and Acuitas’ lipid nanoparticle […]